This year, as in past years, we’ve found inspiring stories and innovative research. All are blazing new trails as they attempt to answer some of the biggest questions in science and medicine.
Meet the 2026 #STATWunderkinds!
statnews.com/wunderkinds/
Missouri AG told Lilly to stop forcing hospitals to provide claims data to receive discounted medicines under 340B, a sign more states are pushing back against drugmakers. trib.al/ozKm4JV
A cow got gene therapy. Patients are still waiting. statnews.com/2026/10/27/gene…
Artiva Biotherapeutics said that it’s winding down after two patients died in a trial testing its cell therapy for autoimmune diseases, the latest in a series of safety events that emerged in a promising research field. bit.ly/4ijeKIV
Recent deaths are setbacks in drug companies’ interest in applying cancer therapy strategies to autoimmune diseases. trib.al/005zYiW
#Breaking: FDA offers new details on quicker approval pathway for personalized gene therapies statnews.com/2026/10/27/fda-…
Rare disease advocates applauded the FDA's move to speed access to treatments. trib.al/EzJF2jR
A gene therapy saved a calf with a rare genetic disease. Years later, Mennonite families work to develop the therapy on their own after biotech ignored it. statnews.com/2026/10/27/gene…
Kennedy on the campaign trail for MAHA, and new rules loom for U.S. investments in Chinese biotech. trib.al/hQn8X1Y
"The question is no longer whether personalized cancer vaccines can work. The question now becomes how to accelerate development and increase access for the patients who could benefit." statnews.com/2026/10/27/canc…
Last year, U.K. gene therapy startup Bloomsbury Genetic Therapies announced it was shutting down after dosing just one patient. Now, a nonprofit is resurrecting its lead program: trib.al/UmLHmsB
STAT retweeted
There is no better reporter anywhere covering rare diseases than STAT's @Jasonmmast. Today, another masterpiece:
Pennsylvania Dutch country, tired of waiting for biopharma, builds drug company of its own statnews.com/2026/10/27/gene…
A U.S. judge rejected a bid to block Eli Lilly from running what Novo Nordisk claims is a “deceptive” advertising campaign about weight loss drugs trib.al/zpdiksB
Brain-eating amoebas are hard to treat and nearly always fatal. But researchers have isolated a compound that could help stop the disease. trib.al/FadSiLO
Brain-eating amoebas are a form of real-world parasites found in warm freshwater.
Infections caused by N. Fowleri are hard to treat and nearly always fatal. But in a new early study, an ocean substance shows treatment promise: trib.al/CzxwBe2
A small community tests if it can solve a crisis no one else could, for the simple reason that they have no other choice. trib.al/RiajHtB
“If we want cancer vaccines to reach patients faster than BRCA testing did, there are several challenges to address now,” write Karen E. Knudsen and Othman Laraki. trib.al/YaiCmHX
“In 2026, the unprecedented pediatric patient crowding of 2022 has become a normal Tuesday,” write Jonathan Kohler and Mary King. trib.al/tqAs8ma
One of the more impressive data sets at this year’s ESMO came from a Roche study of its drug divarasib, which treats lung cancer. trib.al/2JDllwF
The deal would make the Catholic system one of the largest operators of outpatient surgery centers. trib.al/oj9hU0z
The Trump administration removed several security, privacy and transparency requirements for vendors of EHR software. trib.al/3PJ4AiN

