ALT FDA Regulatory Roundtable at the NORD Breakthrough Summit 2026. From left to right, head of the Rare Disease Innovation Hub Amy Comstock Rick (moderator); Michael Davis, MD, PhD, Director, CDER; Michelle E. Tarver, MD, PhD, Director, CDRH; Karim Mikhail, B.Pharm, MSc, Director, CBER.

ALT Rare Impact Award 2026 honoree Mark W. Skinner, JD. Lifetime Achievement Award for advancing bleeding disorders advocacy at the state, national, and international levels, championing patient-centered outcomes research, and serving as an advisor for NORD and other organizations.

ALT Quote from NORD Summit speaker Nicholas Vita, CEO of Apriligen: "What health care investors should be asking is, how do I generate the best risk-adjusted return? And you can't do it anywhere else the way you can in rare disease."

ALT This image is a promotional graphic for the NORD Rare Impact Award. It features the text "Rare Impact Award" and "Youth Leadership" on a blue background, with a photo of a person smiling. The name "Paridhi Tyagi" is displayed below the photo.

ALT All five Lightning Round research presenters on stage at the 2026 NORD Summit

ALT Quote from BioMarin President and CEO Alexander Hardy at the NORD Breakthrough Summit: "There are a lot of biotechs working in rare disease, and that's fantastic, but there are advantages to scale in terms of manufacturing know-how, regulatory expertise, clinical study design, and developing novel endpoints."

ALT Quote from Tarek Rabah, President and CEO of Otsuka North America Pharmaceutical, at the NORD Breakthrough Summit: "The biggest breakthroughs happen where patients have been waiting the longest, where the science is the hardest, and where the risks are probably the highest. But that's also where the biggest reward is."

ALT Panelists on stage at the 2026 NORD Breakthrough Summit CEO Leadership Dialogue hosted by CNBC's Becky Quick, right.

ALT Live quote from the NORD Summit from Tracy Hart of the Osteogenesis Imperfecta Foundation, "It's really important to have the right people on your medical advisory councils and professional advisory groups... people who are not only experts but who understand these issues and are able to navigate them."

ALT NIH Director Dr. Jay Bhattacharya addressing rare disease leaders at the 2026 NORD Breakthrough Summit

ALT Acting FDA Commissioner Kyle Diamantas speaking with NORD President and CEO Pam Gavin at the 2026 NORD Summit.

ALT NORD IAMRARE registry leaders posing for a group photo on the staircase at the 2026 NORD Breakthrough Summit

ALT NORD CEO Pamela Gavin at the 2026 NORD Summit

ALT NORD's State Policy Associate Director Carolyn Sheridan presenting at a meeting of 24 Rare Disease Advisory Councils held at the 2026 NORD Breakthrough Summit

ALT Two representatives of Georgia's Rare Disease Advisory Council

ALT Left and right, two representatives of Montana's Rare Disease Advisory Council. Center, one representative of Florida's Rare Disease Advisory Council.

ALT Map of the United States titled, "What state do you represent?" with pins across 24 states, at the NORD Breakthrough Summit meeting of state Rare Disease Advisory Councils.

ALT A promotional image for Medlive Crossfire, sponsored by Regeneron, titled "Redefining Control Through Innovative Therapies in gMG." It features Katherine Ruzhansky, MD, MS, from the Medical University of South Carolina, and Michael Pulley, MD, PhD, from the University of Florida College of Medicine – Jacksonville. The content is in collaboration with NORD.

ALT A collection of circular buttons with zebra patterns and phrases like "I ❤ Someone Rare" on an orange background. The text reads "Rare Disease Day 2027 Kick Off Webinar" and includes the date and time, Nov. 18, 4 P.M. ET. The logos of NORD and Rare Action Network are at the bottom.