@BluePrintOrphan

Proven excellence in #orphandrug data analytics, forecasting, ​and market access strategy with a special focus in #RareDiseases *retweets/likes ≠ endorsements*

blueprintorphan.com
Joined August 2016
  • Tweets403
  • Following1.4K
  • Followers269
8Media
The #NORDSummit will bring #raredisease leaders & stakeholders together to provide new approaches & fresh perspectives on #publicpolicy, clinical trials, access to #diagnostic testing & pharmaceutical innovation. Register or apply for a scholarship: bit.ly/2WJ7ziE
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BluePrint Orphan retweeted
Allucent@Allucent_CRO3 Jul 2020
Join our experts for a free webinar: The Value of Orphan Drug Designation in your Drug Development Program ow.ly/9KBx50AmOra #OrphanDrug #RareDisease #ClinicalDevelopment #Regulatory #FreeWebinar #ClinialTrials #ClinicalStudies #Innovation Cato Research
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With the #DISORDER: The #RareDisease Film Festival postponed by the pandemic, the Rare Outreach Coalition decided to start its own streaming channel and bring their content right into your home! Read more: bwnews.pr/2Obbpww
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BluePrint Orphan retweeted
RARE Foundation@RareAdvocates29 Jun 2020
LAST CALL to register for #RareAcrossAmerica Check out this article from @healourskin where Shannon von Felden, #RDLA program director, shares everything you need to know about this unique event. issuu.com/healours…/docs/ippf-100-spring-20-issuu/26
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Join #NORD, @CPathInstitute, @US_FDA and @TakedaPharma tomorrow, June 24 at 2:00 PM ET for “Shortening the Timeline for Developing New Treatments – How the Rare Disease Cures Accelerator–Data and Analytics Platform Can Help.” Register: bit.ly/2Bxd10k #RDCADAP #webinar
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BluePrint Orphan retweeted
Global Genes@GlobalGenes26 May 2020
Hoping to improve the treatment experience of people with #rarediseases, @CSLBehring and @Brightinsightco pair up to regulate digital health offerings. ow.ly/bXxI50zL4q5
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HAPPENING TOMORROW: NORD's #RareAction Network will host 2 #COVID19 virtual discussion groups in #NC, #Kansas & #Nebraska. Be a part of the discussion! Join the #raredisease community in your state to share concerns, connect & hear updates. More: bit.ly/3eTU4Ep
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BluePrint Orphan retweeted
Alexion@AlexionPharma20 Apr 2020
As we move quickly to initiate our #COVID19 trial, we also remain committed to serving the patients who currently rely on our medicines and providing continuous supply to these patients.
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What an incredible way to close out #RareDiseaseDay 2019 in the United States! Thank you @EmpireStateBldg for lighting up New York City in honor of the biggest day of the year for 350 million people around the globe impacted by #rarediseases. #ShowYourStripes #ShowYourRare
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#WednesdayWisdom: There are 25-30 million Americans impacted by #rarediseases. Make sure to help spread the word & #ShowYourStripes by getting involved in #RareDiseaseDay! Visit rarediseaseday.us to learn more.

NORD Rare Disease Day | Official US Partner

The National Organization for Rare Disorders (NORD) is proud to be the official US partner for Rare Disease Day.

rarediseases.org
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BluePrint Orphan retweeted
Rare Disease Report@RareDR27 Jun 2018
The @US_FDA has approved @ArrayBiopharma's encorafenib and binimetinib (BRAFTOVI and MEKTOVI) in combination for patients with unresectable or #metastaticmelanoma with a BRAF V600E or V600K mutation as detected by an FDA-approved test. READ: raredr.com/link/3604
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BluePrint Orphan retweeted
Rare Disease Report@RareDR25 Jun 2018
The @US_FDA has granted #Pharmacyclics LLC, @abbvie, and @JanssenUS Priority Review for a supplemental New Drug Application (#sNDA) for the Waldenström's macroglobulinemia combination therapy. READ: raredr.com/link/3595
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BluePrint Orphan retweeted
TechCrunch
@TechCrunch25 Jun 2018
With CBD, marijuana-based medicine gets its first greenlight from the FDA tcrn.ch/2Kb2Ody by @tayhatmaker
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BluePrint Orphan retweeted
HCPLive
@HCPLiveNews22 Jun 2018
#FDA grants #OrphanDrug designation to a treatment for #NecrobiosisLipoidica a skin condition associated with #diabetes mdmag.com/medical-news/fda-g…
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BluePrint Orphan retweeted
Rare Disease Report@RareDR19 Jun 2018
In honor of #WorldSickleCellDay we’ve rounded up the big treatment advances made this year thus far for #sickle cell disease. Check them out: raredr.com/link/3582
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BluePrint Orphan retweeted
Rare Disease Report@RareDR13 Jun 2018
BREAKING: @US_FDA approves #bevacizumab in combination with #chemotherapy for certain patients with ovarian, fallopian tube, or primary peritoneal cancer raredr.com/link/3563
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BluePrint Orphan retweeted
Rare Disease Report@RareDR7 Jun 2018
The @US_FDA has approved @genentech's rituximab (Rituxan) for the treatment of adults with moderate to severe pemphigus vulgaris, a rare and potentially deadly skin disease. READ: raredr.com/link/3548
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FDA Grants Rare Pediatric Disease Designation to Cellectar Biosciences’ #CLR131 for the Treatment of #Rhabdomyosarcoma - bit.ly/2kP5Xka
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"The need for treatment personalization is obvious as every #cancer is molecularly unique," said Dr. Wolfgang Wick. @ArthurBrodsky discusses treatment personalization & more in his Day 1 #ASCO18 recap. bit.ly/2HbqhVz
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BluePrint Orphan retweeted
Protalex, Inc.@ProtalexInc17 Aug 2017
.@US_FDA Office of Orphan Products Development has awarded $PRTX a $403k grant to support future dvlpt of PRTX-100 bit.ly/2v4RHGL
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