
Lab of Dr. Stephanie Cherqui @UCSDHealth. Developing stem cell and gene therapy strategies for degenerative multi-systemic disorders.
La Jolla, California
Joined October 2022
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Cherqui Lab retweeted
@CIRMnews is a proud sponsor of the Gene Therapy Initiative Symposium at @UCSDHealth, which bring together researchers and industry experts to share scientific discoveries and boost collaboration to advance cell and gene therapy treatments for patients everywhere. #gtiUCSD
Cherqui Lab retweeted
Check out this report from @CherquiLab et al. "Rescue of Alzheimer's disease phenotype in a mouse model by transplantation of wild-type hematopoietic stem and progenitor cells", published in @CellReports #ASGCT2024 hubs.li/Q02wFqBN0
Cherqui Lab retweeted
Excited to kick off @WORLDSymposia lysosomal disease conference this year by attending an important @CureSanfilippoF meeting on leveraging data to advance Sanfilippo therapeutic development! #lysosomes #genetherapy #hspc #sanfilippo #mps @UCSDHealth @MPSSociety
Cherqui Lab retweeted
Excited to be at the @MPSSociety 37th Annual Family Conference to present some of my work at @CherquiLab on gene modified HSPC for MPSIIIC! @UCSDHealth #GeneTherapy #StemCells
Cherqui Lab retweeted
Out now in @CellReports, Dr. Stephanie Cherqui's (@Cherqui_S) lab shows hematopoietic #StemCell transplants can protect against memory loss, neuroinflammation and β-amyloid build-up in a mouse model of #AlzheimersDisease 🧠
today.ucsd.edu/story/stem-ce…
Cherqui Lab retweeted
EXCITING STUDY! In new proof-of-concept study, Priyanka Mishra, Stephanie Cherqui et al. show #StemCell transplants may also be promising therapeutic against #AlzheimersDisease. @CherquiLab @ucsdstemcell @ljiresearch @CellReports
doi.org/10.1016/j.celrep.202…
today.ucsd.edu/story/stem-ce…
Cherqui Lab retweeted
Honoured to have been awarded one of the @ASGCTherapy 2023 outstanding poster award for my abstract on my work in the @CherquiLab @UCSDHealth on Hematopoeitic #stemcell #genetherapy for MPSIIIC funded by @MPSSociety & @CureSanfilippoF
Cherqui Lab retweeted
Happy to be back presenting a poster at the @ASGCTherapy annual meeting on my work at @CherquiLab on #stemcell #GeneTherapy for Sanfilippo C funded by @MPSSociety & @CureSanfilippoF. Poster No. 649
Cherqui Lab retweeted
🎧 NEW PODCAST 🎧 Professor @Cherqui_S is a pioneer in the field of #CRISPR cell and gene therapies. She speaks about her work on curing genetic diseases such as Friedreich's ataxia, obstacles in clinical development, and the future of CRISPR therapies 👉 hubs.li/Q01HM8kb0
Cherqui Lab retweeted
I am very happy and grateful to have received the fellowship award from the @CureSanfilippoF to continue my work investigating the use of #stemcell #genetherapy to treat Sanfilippo type C in the @CherquiLab @UCSDHealth
Cherqui Lab retweeted
Congratulations to all of the recipients, including @AquilanoKatia, @Cherqui_S, and @USFHealth
Together, we will #SlowStopReverse and #CureFA
Cherqui Lab retweeted
Professor Stephanie Cherqui of @UCSDMedSchool speaks to us about a prestigious grant from the California Institute for Regenerative Medicine, which will allow her team to bring a new CRISPR therapy for Friedreich’s ataxia to the clinic.
Read more here: bit.ly/3WxA2nV

ALT Stephanie Cherqui Ph.D is an Associate Professor in the Department of Paediatrics, Division of Genetics at the University of California San Diego. Her team is developing therapeutic strategies based on gene-edited haematopoietic stem and progenitor cell transplantation to treat Friedreich’s ataxia and other multi-systemic degenerative disorders. Photo courtesy of Stephanie Cherqui
Cherqui Lab retweeted
Great talks on Clinical Trials in Gene Therapy at the @FranceScience French/American Innovation Days. Organized by the indomitable Stephanie Cherqui @UCSDHealthSci
Cherqui Lab retweeted
Gene Yeo is speaking about engineered RNA-targeting gene therapy approaches at FAID. Join tomorrow to hear from Sanford Stem Cell Institute experts Catriona Jamieson and Dan Kaufman.
@CherquiLab
Cherqui Lab retweeted
The Clinical Trials in Gene Therapy FAID, co-organized by Stephanie Cherqui, is starting now. Experts Alysson Muotri, Sandip Patel, and Gene Yeo from Sanford Stem Cell Institute are speaking today.
@CherquiLab
Cherqui Lab retweeted
Today is World Sanfilippo Awareness Day a day to raise awareness and honour the children living with this devastating disease. @CureSanfilippoF are dedicated to increasing awareness. Learn more about Sanfilippo at curesanfilippofoundation.org…
#WorldSanfilippoDay #CureSanfilippo
Cherqui Lab retweeted
AVROBIO announces sixth and final patient dosed in first #GeneTherapy trial for #cystinosis: bit.ly/3UgzFhy
Thank you #cystinosis community, Dr. Cherqui and @UCSanDiego, the clinical trial team and our AVRO crewmates for your efforts.
#AVROAdvancing




















